Splicing modifier intended to deal with SMA attributable to mutations in chromosome 5q that cause survival motor neuron (SMN) protein deficiency. Evrysdi is administered day-to-day at your home in liquid type by mouth or by feeding tube. This mutation triggers exon 7 being skipped during pre-mRNA processing, resulting in the https://angelinad085sxc8.theblogfairy.com/profile